Inborn Errors Working Party (IEWP)

Ongoing IEWP Studies

Please find a continually updated list of IEWP studies

If you want to contribute to these studies please contact for details.

study subject

status

HSCT in patients with IFN-gamma receptor  deficiency

recruiting

HSCT in adolescents and young adults with PID

closed

mismatched donor HSCT in patients with PID

closed

HSCT in patients with mevalonate kinase deficiency

recruiting

second allogeneic HSCT in PID patients

opening soon